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Join the GM1 Patient Network to accelerate treatment for GM1 Gangliosidosis!

The health information of those impacted by GM1 Gangliosidosis is essential to advancing medical research and for drug developers working to translate research to the clinic and to treat patients.

Help build momentum by joining this shared network!  Patient advocacy organizations and clinicians, and the GM1 community at large can help build a comprehensive database of de-identified data.  This data is an extremely valuable tool for understanding the patient population and to help plan clinical trials.  Furthermore, patients can receive useful information regarding clinical trials as they become available.

Promising research is advancing and this network will help amplify patient voices and help advance the drug development process.  Please provide as much information as possible to move research forward from bench to bedside!

Research is advancing on multiple fronts globally. We must contribute in any way possible to bring these treatments forward. In every second that goes by, the world could be closer to an end of GM1 and to the end of conditions like GM1. Innocent children who have the incredible misfortune of receiving disease-causing genes could have a chance at life.   Please help now!


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The GM1 Patient Network's mission is to advocate for a treatment or cure for GM1 Gangliosidosis.

This registry will serve as a global and shared resource. Launching now, based on the largest registry of GM1 patients in the world, we will build and expand this registry to include as many participants as possible.


By coming together, we not only demonstrate our unity towards a cure but offer researchers and industry the most efficient and uniform source for patient data to advance all treatments.


Join us today. Plus during account set-up, you will have the chance to join the Cure GM1 mailing list and receive messages about relevant developments and clinical trial opportunities.


If you have any questions about participating in the GM1 Patient Network, please Contact Us at